Advertisement
PTC Therapeutics Granted Marketing Authorization By EU For Upstaza To Treat AADC Deficiency
(RTTNews) - PTC Therapeutics, Inc. (PTCT) announced Wednesday that Upstaza (eladocagene exuparvovec) was granted marketing authorization by the European Commission. Upstaza is the first approved disease-modifying treatment for aromatic L-amino acid decarboxylase (AADC) deficiency and the first marketed gene therapy directly infused into the brain. It is approved for patients 18 months and older.
Upstaza is a one-time gene replacement therapy indicated for the treatment of patients aged 18 months and older with a clinical, molecular, and genetically confirmed diagnosis of AADC deficiency with a severe phenotype.
The marketing authorization is applicable to all 27 European Union member states, as well as Iceland, Norway and Liechtenstein.
For More Such Health News, visit rttnews.com
read more
FDA Approves PTC's Kebilidi As First Gene Therapy To Treat AADC Deficiency
The U.S. Food and Drug Administration approved PTC Therapeutics, Inc.'s Kebilidi (eladocagene exuparvovec-tneq) gene therapy for the treatment of aromatic L-amino acid decarboxylase or AADC deficiency. Kebilidi is the first FDA-approved gene therapy for the deficiency. PTC shares gained around 8.5 percent in the extended trading on the Nasdaq on Thursday.
RTTNews
|
hace 180
PTC Therapeutics Says European Commission Returns Translarna Opinion To CHMP For Re-evaluation
PTC Therapeutics, Inc. (PTCT) announced Monday that the European Commission (EC) has decided not to adopt the CHMP's negative opinion of January 24, 2024 on the annual renewal of the conditional marketing authorization of Translarna (ataluren) and has returned the opinion to the CHMP for re-evaluation.
RTTNews
|
hace 358
Japanese Market Notably Lower
The Japanese stock market is trading notably lower on Wednesday after opening in the green, snapping a four-session winning streak, following the mixed cues from Wall Street overnight. The Nikkei 225 is falling to near the 37,900 level, with weakness in exporters and automaker stocks partially offset by gains in technology and financial stocks.
RTTNews
|
hace 16 minutos
Higher Open Anticipated For Indonesia Shares
Ahead of long holiday weekend for Wesak Day, the Indonesia stock market had bounced higher again, one session after ending the eight-day winning streak in which it had rallied more than 210 points or 3.2 percent. The Jakarta Composite Index now rests just above the 6,830-point plateau and it's looking at a solid lead for Wednesday's trade.
RTTNews
|
hace 18 minutos
Mild Rebound Tipped For Hong Kong Shares
The Hong Kong stock market on Tuesday ended the eight-day winning streak in which it had surged almost 1,600 points or 7.1 percent. The Hang Seng Index now sits just beneath the 23,110-point plateau although it may tick back to the upside again on Wednesday.
RTTNews
|
hace 33 minutos
Australian Market Slightly Lower
Australian shares are trading slightly lower on Wednesday, snapping a five-session winning streak, with the benchmark S&P/ASX 200 staying well below the 8,300 level, following the mixed cues from Wall Street overnight, with a mixed performance across most sectors. Traders are also booking some profits following the recent upside in the markets.
RTTNews
|
hace 40 minutos
China Bourse Tipped To Open In The Green
The China stock market has moved higher in consecutive trading days, improving almost 35 points or 1 percent along the way. The Shanghai Composite Index now rests just beneath the 3,375-point plateau and it's looking at a higher open again on Wednesday.
RTTNews
|
hace 48 minutos
Tech Shares May Boost Taiwan Stock Market
The Taiwan stock market has moved higher in three straight sessions, collecting almost 800 points or 4 percent in that span. The Taiwan Stock Exchange now sits just above the 21,330-point plateau and it's likely to open to the upside again on Wednesday.
RTTNews
|
hace 1h 18min
